Goal 2: Reduce Human Disease

Curing Mendelian Disease

Can CRISPR/Cas be utilized to treat human disease? What is necessary to use recent advances in genetic technology, such as CRISPR/Cas, to treat human disease?

Tags (Keywords associated with the idea)

Is this idea a Compelling Question (CQ) or Critical Challenge (CC)? : Compelling Question (CQ)

Details on the impact of addressing this CQ or CC :

It would inspire the staff, electrify the media, and attract the support needed to complete the task.

Feasibility and challenges of addressing this CQ or CC :

The technology has arrived, NHLBI can provide the leadership.

Challenges are many, but surmountable.

Name of idea submitter and other team members who worked on this idea : NHLBI Staff


3 net votes
13 up votes
10 down votes
Idea No. 232